HTA challenges for appraising rare disease interventions viewed through the lens of an institutional multidimensional value framework.

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Abstract

Evaluating rare disease interventions poses challenges for HTA agencies, including uncertainties and ethical issues and tensions. INESSS has recently adopted a Statement of Principles and Ethical Foundations which proposes a multidimensional approach to value appraisal as well as five principles to frame the evaluation process.

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Author and article information

Journal

Journal ID (iso-abbrev): Expert Rev Pharmacoecon Outcomes Res

Title: Expert review of pharmacoeconomics & outcomes research

Publisher: Informa UK Limited

ISSN (Electronic): 1744-8379

ISSN (Print): 1473-7167

Publication date (Electronic): Feb 2023

Volume: 23

Issue: 2

Affiliations

[1 ] Bureau - Méthodologies et éthique, Institut national d'excellence en santé et en services sociaux (INESSS), 2021 Avenue Union, bureau 1200; Montréal H3A 2S9, Quebec, Canada.

[2 ] School of Public Health, Department of Management, Evaluation and Health Policy, Université de Montréal; 7101, avenue du Parc, 3e étage H3N 1X9 Montréal, Quebec, Canada.

[3 ] School of Public Health, Department of Social and Preventive Medicine, Université de Montréal, 7101avenue du Parc, 3e étage H3N 1X9 Montréal, Quebec, Canada.

[4 ] Institut national d'excellence en santé et en services sociaux (INESSS), 2021 Avenue Union, bureau 1200; Montréal H3A 2S9, Québec, Canada.

Article

DOI: 10.1080/14737167.2023.2161513

PubMed ID: 36542763

SO-VID: 23547700-aae5-4540-8091-1ba2a1f10d65

History

Keywords: rare diseases,multidimensional,HTA,Challenge,value framework,value appraisal

Data availability:

Keywords: rare diseases, multidimensional, HTA, Challenge, value framework, value appraisal

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